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Cell culture model Fibrosis RNA splicing Duchenne muscular dystrophy Myotonic dystrophy mouse models Acetylcholinesterase knockout mouse DMPK DM1 Expression Gene editing Astrocytes Myotonic Dystrophy Type 1 CRISPR/Cas9 Heart failure MBNL ARN Myotonic dystrophy type 1 Mice Oligodendrocyte Quantitative microdialysis Central nervous system Aging Maximal force Gene Therapy Autophagy Oligodendrocytes Knockout Skeletal muscle Male Antisense oligonucleotides Therapy Acute coronary syndrome Glial cells Endurance training Muscle GSK3␤ Transgenic mouse model Thérapie génique Brain Cytoskeleton Antisense oligonucleotide Brain dysfunction RNA biology Myotonic Dystrophy type 1 Dystrophie myotonique Cell penetrating peptide Cardiac muscle Muscular dystrophy Animals Myotonic Dystrophy Mouse model PCR Myostatin RNA interference AAV Centronuclear myopathy Trinucleotide Repeat Expansion Astrocyte Cell model Glucocorticoid-receptor CONGENITAL MYATHENIC SYNDROME PacBio BIOLOGIE MOLECULAIRE Genotype phenotype correlation Glutamate Transgenic mouse KNOCKOUT MICE Exercice Long read sequencing Intermediate filament Gene therapy ACETYLCHOLINESTERASE GABA CTG repeat instability Neuron Motoneuron Desmin Dynamin 2 Acetylcholinesterase deficiency Humans CTG repeats Exercise Dystrophie Myotonique Hypoxia In vivo Diaphragm Mouse models Heart Alternative splicing Glucocorticoids Myelin Dystrophin Transcriptomics CTG repeat contractions Dilated cardiomyopathy DMSXL mice CMS Trinucleotide repeat expansion Myotonic dystrophy CRISPRi